Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Genetic Services Laboratory, |
RCV000146417 | SCV000193703 | pathogenic | Severe X-linked myotubular myopathy | 2013-02-08 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000146417 | SCV001392378 | pathogenic | Severe X-linked myotubular myopathy | 2022-02-10 | criteria provided, single submitter | clinical testing | This premature translational stop signal has been observed in individuals with myotubular myopathy (PMID: 10063835, 11793470, 12522554). For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 158938). This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Arg486*) in the MTM1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in MTM1 are known to be pathogenic (PMID: 9305655, 10063835). |