Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000254935 | SCV000322249 | pathogenic | not provided | 2016-02-18 | criteria provided, single submitter | clinical testing | The E17X pathogenic variant in the MTM1 gene has been reported previously in association with myotubular myopathy (Laporte et al., 1997; Biancalana et al., 2003). This variant is predicted to cause loss of normal protein function either through protein truncation or nonsense-mediated mRNA decay. The E17X variant was not observed in approximately 6,500 individuals of European and African American ancestry in the NHLBI Exome Sequencing Project, indicating it is not a common benign variant in these populations. We interpret E17X as a pathogenic variant. |
Labcorp Genetics |
RCV005090298 | SCV005842375 | pathogenic | Severe X-linked myotubular myopathy | 2024-05-10 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Glu17*) in the MTM1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in MTM1 are known to be pathogenic (PMID: 9305655, 10063835). This variant is not present in population databases (gnomAD no frequency). This premature translational stop signal has been observed in individual(s) with X-linked myotubular myopathy (PMID: 9305655). ClinVar contains an entry for this variant (Variation ID: 265397). For these reasons, this variant has been classified as Pathogenic. |