Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000670332 | SCV000795172 | pathogenic | Methylmalonic aciduria due to methylmalonyl-CoA mutase deficiency | 2017-10-30 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001861791 | SCV002243480 | pathogenic | not provided | 2023-11-06 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (Splice site) in the MUT gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in MUT are known to be pathogenic (PMID: 15781192). This variant is present in population databases (rs771542321, gnomAD 0.0009%). This premature translational stop signal has been observed in individual(s) with methylmalonic acidemia (PMID: 16281286). This variant is also known as c.1332+1delG. ClinVar contains an entry for this variant (Variation ID: 554656). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. For these reasons, this variant has been classified as Pathogenic. |
Fulgent Genetics, |
RCV000670332 | SCV002811025 | pathogenic | Methylmalonic aciduria due to methylmalonyl-CoA mutase deficiency | 2022-04-26 | criteria provided, single submitter | clinical testing | |
Gene |
RCV001861791 | SCV003805436 | pathogenic | not provided | 2023-02-22 | criteria provided, single submitter | clinical testing | Canonical splice site variant expected to result in aberrant splicing, although in the absence of functional evidence the actual effect of this sequence change is unknown.; Not observed at significant frequency in large population cohorts (gnomAD); This variant is associated with the following publications: (PMID: 26672496, 27233228, 25959030, 32754920, 16281286, 21048060) |
Prevention |
RCV004752987 | SCV005361003 | pathogenic | MMUT-related disorder | 2024-04-29 | no assertion criteria provided | clinical testing | The MMUT c.1332+1delG variant is predicted to result in a deletion affecting a canonical splice site. This variant has been reported along with a second causative MMUT variant in multiple individuals with isolated methylmalonic acidemia (Worgan et al. 2006. PubMed ID: 16281286; Hörster et al. 2020. PubMed ID: 32754920). This variant is reported in 0.00088% of alleles in individuals of European (Non-Finnish) descent in gnomAD. This variant is interpreted as pathogenic. |