Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratory for Molecular Medicine, |
RCV004018243 | SCV004848916 | likely pathogenic | Hypertrophic cardiomyopathy | 2023-02-02 | criteria provided, single submitter | clinical testing | The p.Asp48X in MYBPC3 has not been reported in individuals with hypertrophic cardiomyopathy and was absent from large population databases. This nonsense variant leads to a premature termination codon at position 48, which is predicted to lead to a truncated or absent protein. Loss of function of the MYBPC3 gene is an established disease mechanism hypertrophic cardiomyopathy. In summary, although additional studies are required to fully establish its clinical significance, this variant meets criteria to be classified as likely pathogenic for autosomal dominant hypertrophic cardiomyopathy. ACMG/AMP criteria applied: PVS1, PM2_Supporting. |