Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV003768167 | SCV004581553 | pathogenic | Mucopolysaccharidosis, MPS-III-B; Charcot-Marie-Tooth disease axonal type 2V | 2022-12-23 | criteria provided, single submitter | clinical testing | This premature translational stop signal has been observed in individual(s) with Sanfilippo syndrome (PMID: 32447333). This sequence change creates a premature translational stop signal (p.Trp103*) in the NAGLU gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in NAGLU are known to be pathogenic (PMID: 9832037, 10094189, 16151907). This variant is not present in population databases (gnomAD no frequency). ClinVar contains an entry for this variant (Variation ID: 590818). For these reasons, this variant has been classified as Pathogenic. |
Sing |
RCV000721982 | SCV000853136 | likely pathogenic | Mucopolysaccharidosis, MPS-III-B | 2017-06-07 | no assertion criteria provided | curation |