Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001905708 | SCV002156048 | uncertain significance | Niemann-Pick disease, type C1 | 2022-09-27 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with cysteine, which is neutral and slightly polar, at codon 714 of the NPC1 protein (p.Arg714Cys). The frequency data for this variant in the population databases is considered unreliable, as metrics indicate poor data quality at this position in the gnomAD database. This variant has not been reported in the literature in individuals affected with NPC1-related conditions. ClinVar contains an entry for this variant (Variation ID: 1386174). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt NPC1 protein function. Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. |
Mayo Clinic Laboratories, |
RCV002261404 | SCV002541455 | uncertain significance | not provided | 2022-01-03 | criteria provided, single submitter | clinical testing | |
Prevention |
RCV004749766 | SCV005361198 | uncertain significance | NPC1-related disorder | 2024-04-24 | no assertion criteria provided | clinical testing | The NPC1 c.2140C>T variant is predicted to result in the amino acid substitution p.Arg714Cys. To our knowledge, this variant has not been reported in the literature. This variant is reported in 0.0045% of alleles in individuals of African descent in gnomAD. At this time, the clinical significance of this variant is uncertain due to the absence of conclusive functional and genetic evidence. |