Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
3billion | RCV001807957 | SCV002058277 | pathogenic | Niemann-Pick disease, type C1 | 2022-01-03 | criteria provided, single submitter | clinical testing | Stop-gained (nonsense): predicted to result in a loss or disruption of normal protein function through nonsense-mediated decay (NMD) or protein truncation. Multiple pathogenic variants are reported downstream of the variant (PVS1_VS). It is not observed in the gnomAD v2.1.1 dataset (PM2_M). Patient’s phenotype is considered compatible with NPC1-related disorder (PP4_P). Therefore, this variant is classified as pathogenic according to the recommendation of ACMG/AMP guideline. |
Ambry Genetics | RCV002541460 | SCV003611712 | pathogenic | Inborn genetic diseases | 2022-04-27 | criteria provided, single submitter | clinical testing | The c.2847G>A (p.W949*) alteration, located in exon 19 (coding exon 19) of the NPC1 gene, consists of a G to A substitution at nucleotide position 2847. This changes the amino acid from a tryptophan (W) to a stop codon at amino acid position 949. This alteration is expected to result in loss of function by premature protein truncation or nonsense-mediated mRNA decay. This variant was not reported in population-based cohorts in the Genome Aggregation Database (gnomAD). Based on the available evidence, this alteration is classified as pathogenic. |