Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000020229 | SCV000220329 | likely pathogenic | Niemann-Pick disease, type C1 | 2014-05-19 | criteria provided, single submitter | literature only | |
Gene |
RCV000413372 | SCV000491260 | pathogenic | not provided | 2023-05-23 | criteria provided, single submitter | clinical testing | Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 19609713, 19307542, 26984608, 20301473, 26910362, 25665455, 31589614, 35892469, 11333381, 28710748, 25349751, 16126423) |
Labcorp Genetics |
RCV000020229 | SCV001391207 | pathogenic | Niemann-Pick disease, type C1 | 2025-01-27 | criteria provided, single submitter | clinical testing | This sequence change replaces glycine, which is neutral and non-polar, with arginine, which is basic and polar, at codon 992 of the NPC1 protein (p.Gly992Arg). This variant is present in population databases (rs80358254, gnomAD 0.003%). This missense change has been observed in individuals with Niemann-Pick disease type C (PMID: 11333381, 20718790, 25349751, 26910362). ClinVar contains an entry for this variant (Variation ID: 21137). Invitae Evidence Modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) indicates that this missense variant is expected to disrupt NPC1 protein function with a positive predictive value of 95%. This variant disrupts the p.Gly992 amino acid residue in NPC1. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 9634529, 16778374). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. For these reasons, this variant has been classified as Pathogenic. |
Revvity Omics, |
RCV000020229 | SCV002018350 | pathogenic | Niemann-Pick disease, type C1 | 2020-04-01 | criteria provided, single submitter | clinical testing | |
Gene |
RCV000020229 | SCV000040572 | not provided | Niemann-Pick disease, type C1 | no assertion provided | literature only | ||
Natera, |
RCV000020229 | SCV002095177 | pathogenic | Niemann-Pick disease, type C1 | 2020-09-25 | no assertion criteria provided | clinical testing |