Total submissions: 7
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Eurofins Ntd Llc |
RCV000594934 | SCV000702740 | uncertain significance | not provided | 2017-12-14 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001248055 | SCV001421519 | uncertain significance | Niemann-Pick disease, type C1 | 2022-10-02 | criteria provided, single submitter | clinical testing | This sequence change replaces alanine, which is neutral and non-polar, with threonine, which is neutral and polar, at codon 181 of the NPC1 protein (p.Ala181Thr). This variant is present in population databases (rs199963560, gnomAD 0.06%). This variant has not been reported in the literature in individuals affected with NPC1-related conditions. ClinVar contains an entry for this variant (Variation ID: 497961). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) has been performed at Invitae for this missense variant, however the output from this modeling did not meet the statistical confidence thresholds required to predict the impact of this variant on NPC1 protein function. In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. |
Victorian Clinical Genetics Services, |
RCV001248055 | SCV002767724 | uncertain significance | Niemann-Pick disease, type C1 | 2024-10-11 | criteria provided, single submitter | clinical testing | Based on the classification scheme VCGS_Germline_v1.1.1, this variant is classified as VOUS – 3B. Following criteria are met: 0102 - Loss-of-function is a known mechanism of disease for this gene. (N) 0106 - This gene is known to be associated with autosomal recessive disease. (N) 0200 - Variant is predicted to result in a missense amino acid change from alanine to threonine. (N) 0251 - Variant is heterozygous. (N) 0304 - Variant is present in gnomAD <0.01 for a recessive condition (34 Heterozygotes, 0 Homozygotes). (P) 0502 - Missense variant with conflicting in-silico predictions and/or uninformative conservation. (N) 0601 - Variant affects at least one well-established (essential) functional domain or motif, NPC1 N terminal subdomain. (Kwon, H. et al. (2009)). (P) 0705 - No comparable variants have previous evidence for pathogenicity. (N) 0804 - Variant has previously been described as variant of uncertain significance in multiple independent cases. (LOVD, ClinVar, Zech, M. et al. (2013)). (N) 0905 - No segregation evidence has been identified for this variant. (N) 1007 - No published functional evidence has been identified for this variant. (N) Legend: (P) - Pathogenic, (N) - Neutral, (B) - Benign |
Fulgent Genetics, |
RCV001248055 | SCV002783825 | uncertain significance | Niemann-Pick disease, type C1 | 2022-02-23 | criteria provided, single submitter | clinical testing | |
Ambry Genetics | RCV002531010 | SCV003545510 | uncertain significance | Inborn genetic diseases | 2022-02-10 | criteria provided, single submitter | clinical testing | The c.541G>A (p.A181T) alteration is located in exon 5 (coding exon 5) of the NPC1 gene. This alteration results from a G to A substitution at nucleotide position 541, causing the alanine (A) at amino acid position 181 to be replaced by a threonine (T). Based on insufficient or conflicting evidence, the clinical significance of this alteration remains unclear. |
Gene |
RCV000594934 | SCV005401522 | uncertain significance | not provided | 2024-05-18 | criteria provided, single submitter | clinical testing | In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; Reported heterozygous in individuals with early-onset Parkinson disease in published literature; however, further clinical information was not provided (PMID: 35861376); This variant is associated with the following publications: (PMID: 35861376, 24386122) |
Natera, |
RCV001248055 | SCV002095228 | uncertain significance | Niemann-Pick disease, type C1 | 2020-01-29 | no assertion criteria provided | clinical testing |