Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV002509875 | SCV002818514 | likely pathogenic | Phenylketonuria | 2022-07-30 | reviewed by expert panel | curation | This c.1023 G>C (p.Lys341Asn) variant in PAH was seen in a patient with mPKU in trans with the pathogenic variant p.Ala434Asp (PMID: 28982351). This variant was found at a very low frequency in population databases. Multiple lines of computational evidence support a deleterious effect. In summary, this variant meets criteria to be classified as likely pathogenic for PAH. PAH-specific ACMG/AMP criteria applied: PM3, PM2, PP3, PP4. |