Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000000651 | SCV001572849 | likely pathogenic | Phenylketonuria | 2019-05-04 | reviewed by expert panel | curation | The c.1092_1106del (p.Leu365_Leu369del) variant in PAH has been reported in 1 individual with PKU (PP4; PMID: 1363837) in trans with pathogenic variant p.R408W (PM3). This variant is absent in population databases (PM2). This variant is a 15 bp in-frame deletion in exon 11 (PM4). In summary, this variant meets criteria to be classified as likely pathogenic for PAH. PAH-specific ACMG/AMP criteria applied: PP4, PM2, PM3, PM4. |
OMIM | RCV000000651 | SCV000020801 | pathogenic | Phenylketonuria | 1992-12-01 | no assertion criteria provided | literature only | |
De |
RCV000088753 | SCV000119337 | not provided | not provided | no assertion provided | not provided |