Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000758108 | SCV000886582 | uncertain significance | Phenylketonuria | 2023-07-23 | reviewed by expert panel | curation | The c.1101G>A (p.Leu367=) variant in PAH is reported in an individual with Classic PKU, in trans with p.R243Q. (PMID: 16256386) This variant is absent in population databases. Two splicing algorthms predict a deleterious effect (Human splicing finder: potential alteration of splicing; MaxEnt scan: +571.94% Variation). In summary, this variant meets criteria to be classified as uncertain significance for PAH. PAH-specific ACMG/AMP criteria applied: PM2_supporting, PM3, PP4, PP3. |
Labcorp Genetics |
RCV000758108 | SCV001601592 | likely benign | Phenylketonuria | 2018-09-04 | criteria provided, single submitter | clinical testing | |
Gene |
RCV000088759 | SCV001986174 | uncertain significance | not provided | 2019-10-28 | criteria provided, single submitter | clinical testing | Not observed in large population cohorts (Lek et al., 2016); Nucleotide substitution has no predicted effect on splicing and is not conserved across species; This variant is associated with the following publications: (PMID: 16256386, 32668217) |
De |
RCV000088759 | SCV000119343 | not provided | not provided | no assertion provided | not provided |