Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000210792 | SCV000886606 | likely pathogenic | Phenylketonuria | 2018-12-10 | reviewed by expert panel | curation | The c.110T>C (p.Leu37Pro) variant in PAH is reported in 1 patient with mild PKU. Assessment of BH4 deficiencies not reported. It was detected with a known pathogenic variant, p.R408W. (PMID: 24350308) This variant is absent from ExAC, gnomAD, 1000G, and ESP. A deleterious effect is predicted in SIFT, Polyphen-2, and MutationTaster. In summary, this variant meets criteria to be classified as likely pathogenic for PAH. PAH-specific ACMG/AMP criteria applied: PM2, PM3, PP4, PP3. |
Department of Prenatal Diagnosis, |
RCV000210792 | SCV000266850 | likely pathogenic | Phenylketonuria | 2013-10-01 | no assertion criteria provided | clinical testing |