Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000000666 | SCV001370838 | pathogenic | Phenylketonuria | 2020-06-26 | reviewed by expert panel | curation | The c.1129delT (p.Tyr377Thrfs) variant in PAH has been reported in an Icelandic PKU cohort. (PP4; PMID: 9450182). This variant is absent from gnomAD (PM2). It is a frameshift variant in exon 11 of 13 in PAH, predicted to undergo nonsense mediated decay with the truncated region critical to protein function (PVS1). In summary, this variant meets criteria to be classified as pathogenic for PAH. PAH-specific ACMG/AMP criteria applied: PVS1, PM2, PP4. |
OMIM | RCV000000666 | SCV000020816 | pathogenic | Phenylketonuria | 1997-11-01 | no assertion criteria provided | literature only | |
De |
RCV000088766 | SCV000119350 | not provided | not provided | no assertion provided | not provided |