Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV002509869 | SCV002818504 | pathogenic | Phenylketonuria | 2022-07-30 | reviewed by expert panel | curation | The nonsense variant c.1176dup (p.Asn393Ter) occurs in exon 11 and is predicted to result in NMD. The variant is absent from population databases. At least one classical PKU patient has been reported (PMID: 20188615) homozygous for this variant. In summary, this variant meets criteria to be classified as Pathogenic for PAH. PAH-specific ACMG/AMP criteria applied: PVS1, PM2, PM3_supporting, PP4. |