Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV002509870 | SCV002818505 | likely pathogenic | Phenylketonuria | 2022-07-30 | reviewed by expert panel | curation | The NM_000277.3(PAH):c.1177_1178insT (p.Asn393IlefsTer2) frameshift variant has not been reported in the literature to our knowledge. This frameshift variant is in exon 11 where it creates a premature stop codon, which is predicted to result in NMD and is absent from population databases. In summary, this variant meets criteria to be classified as likely pathogenic for PAH. PAH-specific ACMG/AMP criteria applied: PVS1 and PM2. |