Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000993594 | SCV001146685 | pathogenic | Phenylketonuria | 2019-02-26 | reviewed by expert panel | curation | The PAH: c.13delG variant is a frameshift variant occurring in exon 1 of 13 in the canonical transcript of PAH, a gene fulfilling the most recent criteria for LOF being a known disease mechanism (see PMID: 30192042) (PVS1). The variant has been previously reported the heterozygous state in 1 Chinese PKU case (PMID: 26503515); no further information regarding the patient's phenotype or the other accompanying allele was given (PP4). It is absent from control databases including ethnically matched individuals, including gnomAD/ExAC, 1000 Genomes, and ESP (PM2). |