Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV002259585 | SCV002540167 | uncertain significance | Phenylketonuria | 2021-02-14 | reviewed by expert panel | curation | The c.175G>T (p.Asp59Tyr) variant in PAH has been reported in 1 individual with mild hyperphenylalaninaemia (BH4 deficiency excluded). (PP4_Moderate; PMID: 10234516). This variant has is absent in population databases. This variant was detected with A403V (Pathogenic in ClinVar) (PM3_supporting; PMID: 10234516). Computational evidence is conflicting. In summary, this variant meets criteria to be classified as uncertain significance for PAH. PAH-specific ACMG/AMP criteria applied: PP4_Moderate, PM2, PM3_supporting. |
De |
RCV000088857 | SCV000119452 | not provided | not provided | no assertion provided | not provided |