Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV001269312 | SCV001448662 | uncertain significance | Phenylketonuria | 2020-09-12 | reviewed by expert panel | curation | The c.510-6T>G variant in PAH is absent from population databases (PM2). It has been observed in at least one classic PKU patient (PMID: 23764561; PP4). The patient is compound heterozygous with pathogenic variant R408W (ClinVar 577; PM3_supporting). In summary, this variant meets criteria to be classified as uncertain significance for PAH. PAH-specific ACMG/AMP criteria applied: PM2, PM3_supporting, PP4. |
De |
RCV000088962 | SCV000119565 | not provided | not provided | no assertion provided | not provided |