Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV004823287 | SCV005442785 | likely pathogenic | Phenylketonuria | 2024-11-17 | reviewed by expert panel | curation | The c.552G>T (p.Lys184Asn) variant in PAH is a missense variant predicted to cause substitution of lysine by asparagine at amino acid 184. It has been detected in a patient with phenylketonuria with pathogenic variant c.442-1G>A, phase unconfirmed (PMID: 25456745). This variant is absent in population databases. Multiple lines of computational evidence support a deleterious effect (REVEL= 0.827). In summary, this variant is classified as likely pathogenic due to insufficient evidence based on the ACMG/AMP criteria applied, as specified by the ClinGen PAH VCEP: PM2_supporting, PM3_supporting, PP3_moderate, PP4_moderate. |