Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV001269337 | SCV001448679 | pathogenic | Phenylketonuria | 2020-10-30 | reviewed by expert panel | curation | The c.584dup PAH variant has been identified in at least one patient with PKU (PMID: 25550961) and is absent from 1000G, ESP, and gnomAD databases. This variant leads to the frameshift Ser196ValfsTer4, creating a stop codon in exon 6 of 13 which is predicted to cause NMD. In summary, this variant meets criteria to be classified as pathogenic for PAH. PAH-specific ACMG/AMP criteria applied: PVS1, PP4, PM2. |