Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000993601 | SCV001146692 | likely pathogenic | Phenylketonuria | 2019-08-11 | reviewed by expert panel | curation | Likely pathogenic: The c. 60+4A>T was reported in two patients with PKU, who carried a second pathogenic variant (PMID: 17502162, parental studies not reported). Further, computational splice site algorithms predict a reduction at the donor site of intron 1. This variant is absent from population databases, including 1000 Genomes, ESP, and gnomAD. In summary, this variant meets criteria to be classified as likely pathogenic for PAH. PAH-specific ACMG/AMP criteria applied: PM3, PM2, PP3, PP4. |