Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000993646 | SCV001146778 | uncertain significance | Phenylketonuria | 2019-04-03 | reviewed by expert panel | curation | The PAH c.60+5_60+6del variant has been reported once in a PKU case, however without indication of a second in trans variant (PMID: 26503515). This variant is absent from the population database gnomAD and results in deletion of moderately conserved bases in the donor splice site of intron 1. Computational analyses (Alamut v.2.11) predict that this variant may impact splicing by weakening the nearby canonical splice site. Altogether, there is not enough evidence to classify the c.60+5_60+6del variant with certainty. PAH-specific ACMG/AMP criteria applied: PP4, PP3, PM2 |