Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV001200001 | SCV001370853 | likely pathogenic | Phenylketonuria | 2020-04-05 | reviewed by expert panel | curation | The c.676C>T (p.Gln226Ter) variant in PAH is a null variant (nonsense variant) in a gene where LOF is a known mechanism of disease, leading to premature truncation and NMD (PVS1). It is absent from ethnically diverse control databases, including gnomAD/ExAC, 1000 Genomes, and ESP (PM2). It does not appear to have been reported in detail in the published literature, but has been noted in the BioPKU database (PMID: 24939588) and in Clinvar (Variation ID 102782), without further case-level information. Classification: Likely Pathogenic Supporting Criteria: PVS1, PM2 |
De |
RCV000089033 | SCV000119638 | not provided | not provided | no assertion provided | not provided |