Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000672289 | SCV000886612 | pathogenic | Phenylketonuria | 2018-12-10 | reviewed by expert panel | curation | The c.800A>G (p.Gln267Arg) variant in PAH has been reported in 1 individual with Classic PKU (BH4 deficiency excluded) and was detected with G257V which is pathogenic per the ClinGen PAH VCEP (PP4_Moderate, PM3; PMID: 24401910). This variant is absent in population databases (PM2). This variant has 1.1% enzyme activity (PS3; PMID: 24401910). Computational prediction tools and conservation analysis suggest that this variant may impact the protein (PP3). In summary, this variant meets criteria to be classified as pathogenic for PAH. PAH-specific ACMG/AMP criteria applied: PP4_Moderate, PS3, PM2, PM3, PP3. |
Counsyl | RCV000672289 | SCV000797384 | uncertain significance | Phenylketonuria | 2018-01-26 | criteria provided, single submitter | clinical testing | |
Juno Genomics, |
RCV000672289 | SCV005418363 | pathogenic | Phenylketonuria | criteria provided, single submitter | clinical testing | PM2_Supporting+PM5+PS3+PM3+PP4_Moderate |