Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000758093 | SCV000886560 | uncertain significance | Phenylketonuria | 2018-12-10 | reviewed by expert panel | curation | The c.817T>C (p.Ser273Pro) variant in PAH has been reported in a Japanese patient with classic PKU. (Biopterin deficiency excluded. PMID: 1114275, PP4_Moderate) It was detected with c.442-2G>A (not in ClinVar). This variant is absent from ExAC, gnomAD, 1000G and ESP. A deleterious effect is predicted in SIFT, Polyphen-2, MutationTaster, and REVEL=0.976. In summary, this variant meets criteria to be classified as uncertain significance for PAH. PAH-specific ACMG/AMP criteria applied: PP4_Moderate, PM2, PP3. |