Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Nx |
RCV001506975 | SCV001653754 | likely pathogenic | Phenylketonuria | 2019-12-02 | criteria provided, single submitter | clinical testing | This variant (c.830_831insC) is predicted to result in a frameshift and premature peptide translation termination or nonsense mediated decay (p.Thr278TyrfsTer5 PVS1). This variant is not found in gnomAD population databases (PM2). Dworniczak et al. (PMID 1363786) describes a frameshift mutation that occurs across this location, c.822_832delGCCCATGTATA that is classified in ClinVar (VCV000102852.3) as pathogenic. We interpret c.830_831insC to be likely pathogenic. |