Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV003479004 | SCV004222632 | pathogenic | Phenylketonuria | 2023-10-15 | reviewed by expert panel | curation | The c.839_840insT (p.Glu280Aspfs) variant in PAH has been reported in an individual with PKU (PP4; 15300621). This variant has is absent from ExAC and gnomAD (PM2_supporting). It is a null variant (frameshift) in exon 7/13 with NMD predicted (PVS1). In summary, this variant meets criteria to be classified as pathogenic for PAH. PAH-specific ACMG/AMP criteria applied: PVS1, PM2_supporting, PP4. |
De |
RCV000089128 | SCV000119737 | not provided | not provided | no assertion provided | not provided |