Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000721176 | SCV000852104 | likely pathogenic | Phenylketonuria | 2018-08-12 | reviewed by expert panel | curation | PAH-specific ACMG/AMP criteria applied: PP3: HSF: Broken WT Donor Site, New Donor Site. MaxEnt: Broken WT Donor Site.; PM2: Absent from ExAC, gnomAD, 1000G, ESP; PP4_Moderate: IVS7+4A>G seen in 2 PKU patients. BH4 deficiency was ruled out. Upgraded per ClinGen PAH EP. (PMID:21147011); PM3: Detected in trans with A300S, pathogenic in ClinVar (PMID:21147011). In summary this variant meets criteria to be classified as likely pathogenic for phenylketonuria in an autosomal recessive manner based on the ACMG/AMP criteria applied as specified by the PAH Expert Panel: (PP3, PM2, PP4_Moderate, PM3). |
Quest Diagnostics Nichols Institute San Juan Capistrano | RCV000506590 | SCV000601719 | uncertain significance | not specified | 2016-08-12 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000721176 | SCV003441007 | pathogenic | Phenylketonuria | 2024-01-26 | criteria provided, single submitter | clinical testing | This sequence change falls in intron 7 of the PAH gene. It does not directly change the encoded amino acid sequence of the PAH protein. It affects a nucleotide within the consensus splice site. This variant is not present in population databases (gnomAD no frequency). This variant has been observed in individuals with hyperphenylalaninemia (PMID: 21147011, 32668217). This variant is also known as IVS7+4A>G. ClinVar contains an entry for this variant (Variation ID: 439228). Variants that disrupt the consensus splice site are a relatively common cause of aberrant splicing (PMID: 17576681, 9536098). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. For these reasons, this variant has been classified as Pathogenic. |
Gene |
RCV004719845 | SCV005326098 | likely pathogenic | not provided | 2023-08-09 | criteria provided, single submitter | clinical testing | Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports a deleterious effect on splicing; This variant is associated with the following publications: (PMID: 25525159, 21147011, 35281663, 32668217) |