Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV002509881 | SCV002818528 | uncertain significance | Phenylketonuria | 2022-12-09 | reviewed by expert panel | curation | This c.843T>A (p.Pro281Pro) variant in PAH was detected with the pathogenic variant c.168+5G>C in a patient with PKU (PMID:26413448). This variant was absent in population databases. This is a synonymous variant which is not predicted to have a splice-altering consequence. In summary, this variant meets criteria to be classified as a variant of unknown significance for PAH. PAH-specific ACMG/AMP criteria applied: BP7, PM3_Supporting, PM2, PP4. |