Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV003316802 | SCV004015302 | likely pathogenic | Phenylketonuria | 2023-03-16 | reviewed by expert panel | curation | The c.970-1G>C variant in PAH occurs within the canonical splice acceptor site of intron 9. This is predicted to cause in-frame skipping of exon 10. It has been detected in a patient with PAH deficiency with second allele not reported (PMID: 31332730). The variant is absent in population databases. In summary, this variant meets criteria to be classified as Likely Pathogenic for PAH deficiency based on this ACMG/AMP criteria applied, as specified by the ClinGen PAH VCEP: PM2, PP4_moderate, PVS1_strong |
Eurofins Ntd Llc |
RCV000731213 | SCV000859000 | pathogenic | not provided | 2018-01-04 | criteria provided, single submitter | clinical testing |