Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
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Hainan Provincial Key Laboratory for Human Reproductive Medicine and Genetic Research | RCV004596592 | SCV004232725 | likely pathogenic | Focal segmental glomerulosclerosis 7 | no assertion criteria provided | clinical testing | We collected retrospective clinical data of the proband and conducted whole exome sequencing (WES) to identify the causative gene. Subsequently, Sanger sequencing was employed to validate the mutation detected by WES in additional family members. The proband (Ⅲ-1) exhibited fetal renal hypodysplasia. WES revealed a novel heterozygous missense variant (c.166C>T, p.Arg56Trp) within the PAX2 gene in the proband, inherited paternally. This mutation affected highly conserved residues and was predicted to disrupt the normal protein structure. Furthermore, the variant co-segregated with the disease phenotypes within the family. The variant was classified as 'likely pathogenic (PM2 + PM5 + PP1 + PP3)' based on the latest ACMG guidelines on sequence variants. The diagnosis of FSGS7 was established, with the identified variant considered causative. |