Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Al Jalila Children’s Genomics Center, |
RCV001733745 | SCV001984611 | uncertain significance | Glycogen storage disease due to phosphoglycerate kinase 1 deficiency | 2020-05-14 | criteria provided, single submitter | clinical testing | |
Gene |
RCV004591560 | SCV005079470 | uncertain significance | not provided | 2023-10-11 | criteria provided, single submitter | clinical testing | Reported previously as a maternally inherited hemizygous variant in an individual with seizures (El Naofal et al., 2023); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 36703223) |