Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Genetics and NGS Laboratory, |
RCV004698813 | SCV005200512 | likely pathogenic | Glycogen storage disease IXa1 | 2024-08-15 | criteria provided, single submitter | clinical testing | Null variant (intronic within ±2 of splice site) in gene PHKA2. Loss-of-function is a known mechanism of disease (gene has 81 reported pathogenic LOF variants) (PVS1). Variant not found in gnomAD genomes. Variant not found in gnomAD exomes (PM2).We observed this variant in hemizygosity in a 5-year-old boy diagnosed with glycogenosis. |