Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratorio de Genetica e Diagnostico Molecular, |
RCV002243545 | SCV002512214 | pathogenic | Glycogen storage disease IXb | 2021-06-21 | criteria provided, single submitter | clinical testing | ACMG classification criteria: PVS1 very strong, PS4 supporting, PM3 moderate |
Labcorp Genetics |
RCV002243545 | SCV003443550 | pathogenic | Glycogen storage disease IXb | 2024-04-23 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Gln191Hisfs*5) in the PHKB gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in PHKB are known to be pathogenic (PMID: 9215682, 9326319). This variant is present in population databases (no rsID available, gnomAD 0.002%). This premature translational stop signal has been observed in individual(s) with glycogen storage disease (PMID: 21646031, 31508908). This variant is also known as c.572_576delAGATT. ClinVar contains an entry for this variant (Variation ID: 1683502). For these reasons, this variant has been classified as Pathogenic. |