Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Centogene AG - |
RCV001250205 | SCV001424474 | likely pathogenic | Glycogen storage disease type IXc | criteria provided, single submitter | clinical testing | ||
Labcorp Genetics |
RCV003770291 | SCV004611955 | pathogenic | Glycogen storage disease IXc | 2023-01-30 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This sequence change creates a premature translational stop signal (p.Arg152*) in the PHKG2 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in PHKG2 are known to be pathogenic (PMID: 8896567, 17689125, 21646031). This variant is present in population databases (rs772912966, gnomAD 0.003%). This premature translational stop signal has been observed in individual(s) with clinical features of PHKG2-related conditions (PMID: 31508908, 32697758). ClinVar contains an entry for this variant (Variation ID: 973563). |
Neuberg Centre For Genomic Medicine, |
RCV003770291 | SCV005690617 | pathogenic | Glycogen storage disease IXc | 2023-06-22 | criteria provided, single submitter | clinical testing | The observed stop gain c.454C>T (p.Arg152Ter) variant in PHKG2 gene has been previously reported in homozygous state in multiple individuals affected with Glycogen storage disease IXc (Waheed N et al. 2020; Kido J et al. 2021). The p.Arg152Ter variant is present with allele frequency of 0.0004% in gnomAD Exomes. This variant has been submitted to the ClinVar database as Likely Pathogenic. Computational evidence (Mutation Taster - Disease causing) predicts damaging effect on protein structure and function for this variant. The reference nucleotide change c.454C>T in PHKG2 is predicted as conserved by GERP++ and PhyloP across 100 vertebrates. This variant is predicted to cause loss of normal protein function through protein truncation. Loss of function variants have been previously reported to be disease causing. For these reasons, this variant has been classified as Pathogenic. In the absence of another reportable variant in PHKG2 gene, the molecular diagnosis is not confirmed. |