Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001851554 | SCV002211341 | pathogenic | not provided | 2021-06-19 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Glu440*) in the PKLR gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in PKLR are known to be pathogenic (PMID: 15953013, 26832193). For these reasons, this variant has been classified as Pathogenic. This variant has been observed in individual(s) with pyruvate kinase deficiency (PMID: 15491302). ClinVar contains an entry for this variant (Variation ID: 1516). This variant is present in population databases (rs771145576, ExAC 0.001%). |
OMIM | RCV000001580 | SCV000021736 | pathogenic | Pyruvate kinase deficiency of red cells | 2004-11-01 | no assertion criteria provided | literature only |