Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Neuberg Centre For Genomic Medicine, |
RCV004720644 | SCV005329406 | pathogenic | Pyruvate kinase deficiency of red cells | 2023-05-20 | criteria provided, single submitter | clinical testing | The observed stop gain c.603G>A (p.Trp201Ter) variant in PKLR gene has been reported previously in compound heterozygous state in an individual affected with pyruvate kinase deficiency (Percy et al. 2007). The c.603G>A variant is absent in gnomAD Exomes database. This variant has not been submitted to the ClinVar database. Computation evidence (Mutation Taster - disease causing) predict a damaging effect on protein structure and function for this variant. The nucleotide change c.603G>A in PKLR is predicted as conserved by GERP++ and PhyloP across 100 vertebrates. This variant is predicted to cause loss of normal protein function through protein truncation. Loss of function variants have been previously reported to be disease causing. For these reasons, this variant has been classified as Pathogenic. |