Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001410012 | SCV001612053 | likely benign | PMM2-congenital disorder of glycosylation | 2023-10-26 | criteria provided, single submitter | clinical testing | |
Neurometabolic Diseases Laboratory, |
RCV001410012 | SCV003920794 | pathogenic | PMM2-congenital disorder of glycosylation | 2023-04-27 | criteria provided, single submitter | research | |
Baylor Genetics | RCV001410012 | SCV004205297 | likely pathogenic | PMM2-congenital disorder of glycosylation | 2023-11-03 | criteria provided, single submitter | clinical testing | |
Gene |
RCV004789580 | SCV005401119 | likely pathogenic | not provided | 2024-05-16 | criteria provided, single submitter | clinical testing | Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports a deleterious effect on splicing; RNA studies demonstrate a damaging effect: c.640-23 A>G results in leaky splicing leading to a proportion of transcripts lacking exon 8 (PMID: 16376131); This variant is associated with the following publications: (PMID: 38587076, 34682117, 16376131, 33643843, 37224763) |