Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000087090 | SCV003443815 | uncertain significance | Combined deficiency of sialidase AND beta galactosidase | 2022-04-04 | criteria provided, single submitter | clinical testing | This sequence change replaces valine, which is neutral and non-polar, with methionine, which is neutral and non-polar, at codon 150 of the CTSA protein (p.Val150Met). This variant is present in population databases (rs137854545, gnomAD 0.003%). This missense change has been observed in individual(s) with galactosialidosis (PMID: 8968752). ClinVar contains an entry for this variant (Variation ID: 383). Algorithms developed to predict the effect of missense changes on protein structure and function are either unavailable or do not agree on the potential impact of this missense change (SIFT: "Not Available"; PolyPhen-2: "Probably Damaging"; Align-GVGD: "Not Available"). Experimental studies have shown that this missense change affects CTSA function (PMID: 8968752). In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. |
OMIM | RCV000000414 | SCV000020558 | pathogenic | Galactosialidosis, early infantile | 1991-12-01 | no assertion criteria provided | literature only | |
Unidad de Diagnostico y Tratamiento de Errores Congenitos del Metabolismo. |
RCV000087090 | SCV000119947 | pathogenic | Combined deficiency of sialidase AND beta galactosidase | no assertion criteria provided | research |