Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001989873 | SCV002236038 | pathogenic | Axenfeld-Rieger syndrome type 1; Anterior segment dysgenesis 4 | 2020-12-28 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This sequence change creates a premature translational stop signal (p.Tyr121*) in the PITX2 gene. While this is not anticipated to result in nonsense mediated decay, it is expected to disrupt the last 151 amino acid(s) of the PITX2 protein. This variant is not present in population databases (ExAC no frequency). This nonsense change has been observed in individual(s) with Axenfeld-Rieger syndrome (PMID: 17167399). This variant disrupts the C-terminus of the PITX2 protein. Other variant(s) that disrupt this region (p.Trp133*) have been determined to be pathogenic (PMID: 8944018, 16498627). This suggests that variants that disrupt this region of the protein are likely to be causative of disease. |
Human Developmental Genetics Laboratory, |
RCV002290812 | SCV002538935 | pathogenic | Axenfeld-Rieger syndrome type 1 | 2022-06-23 | criteria provided, single submitter | research | |
MGZ Medical Genetics Center | RCV002290812 | SCV002581017 | likely pathogenic | Axenfeld-Rieger syndrome type 1 | 2022-08-30 | criteria provided, single submitter | clinical testing |