Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Blueprint Genetics | RCV001073324 | SCV001238863 | likely pathogenic | Retinal dystrophy | 2018-11-20 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001208105 | SCV001379477 | likely pathogenic | Leber congenital amaurosis 2; Retinitis pigmentosa 20 | 2024-01-27 | criteria provided, single submitter | clinical testing | This sequence change replaces isoleucine, which is neutral and non-polar, with threonine, which is neutral and polar, at codon 206 of the RPE65 protein (p.Ile206Thr). This variant is present in population databases (rs768445391, gnomAD 0.003%). This missense change has been observed in individuals with clinical features of autosomal recessive inherited retinal dystrophy (PMID: 32037395; Invitae). ClinVar contains an entry for this variant (Variation ID: 829832). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is not expected to disrupt RPE65 protein function with a negative predictive value of 80%. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. |
Bioscientia Institut fuer Medizinische Diagnostik Gmb |
RCV001029769 | SCV001192547 | likely pathogenic | Retinitis pigmentosa 20 | 2019-04-09 | no assertion criteria provided | clinical testing | |
Natera, |
RCV001836068 | SCV002092765 | uncertain significance | Leber congenital amaurosis | 2020-07-23 | no assertion criteria provided | clinical testing |