Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Institute of Human Genetics, |
RCV000408553 | SCV000281796 | pathogenic | Severe early-childhood-onset retinal dystrophy | 2016-01-01 | criteria provided, single submitter | clinical testing | |
Gene |
RCV000085379 | SCV000890154 | pathogenic | not provided | 2018-08-07 | criteria provided, single submitter | clinical testing | The W41X nonsense variant has been reported previously in association with ABCA4-related disorders (Cideciyan et al., 2009; Schulz et al., 2017). This variant is predicted to cause loss of normal protein function either through protein truncation or nonsense-mediated mRNA decay. The variant is not observed at a significant frequency in large population cohorts (Lek et al., 2016). We consider this variant to be pathogenic. |
Labcorp Genetics |
RCV000085379 | SCV001222994 | pathogenic | not provided | 2022-06-12 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may create or strengthen a splice site. ClinVar contains an entry for this variant (Variation ID: 99036). This premature translational stop signal has been observed in individuals with ABCA4-related retinal dystrophy (PMID: 19074458, 25444351, 30670881). This variant is present in population databases (rs61751410, gnomAD 0.0009%). This sequence change creates a premature translational stop signal (p.Trp41*) in the ABCA4 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in ABCA4 are known to be pathogenic (PMID: 10958761, 24938718, 25312043, 26780318). |
Institute of Medical Genetics and Applied Genomics, |
RCV000085379 | SCV001480161 | pathogenic | not provided | 2021-02-01 | criteria provided, single submitter | clinical testing | |
Retina International | RCV000085379 | SCV000117516 | not provided | not provided | no assertion provided | not provided |