Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000085420 | SCV004292536 | pathogenic | not provided | 2023-08-25 | criteria provided, single submitter | clinical testing | This sequence change affects a donor splice site in intron 12 of the ABCA4 gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in ABCA4 are known to be pathogenic (PMID: 10958761, 24938718, 25312043, 26780318). This variant is not present in population databases (gnomAD no frequency). Disruption of this splice site has been observed in individual(s) with autosomal recessive retinitis pigmentosa and/or Stargardt disease (PMID: 12202497, 31814693). It has also been observed to segregate with disease in related individuals. This variant is also known as IVS12+2T>G. ClinVar contains an entry for this variant (Variation ID: 99076). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. For these reasons, this variant has been classified as Pathogenic. |
Dept Of Ophthalmology, |
RCV003888471 | SCV004705888 | pathogenic | Retinal dystrophy | 2023-10-01 | criteria provided, single submitter | research | |
Fulgent Genetics, |
RCV005031584 | SCV005663518 | pathogenic | Cone-rod dystrophy 3; Age related macular degeneration 2; Severe early-childhood-onset retinal dystrophy; Retinitis pigmentosa 19 | 2024-01-27 | criteria provided, single submitter | clinical testing | |
Retina International | RCV000085420 | SCV000117557 | not provided | not provided | no assertion provided | not provided | ||
Department of Ophthalmology and Visual Sciences Kyoto University | RCV000132587 | SCV000172531 | pathogenic | Severe early-childhood-onset retinal dystrophy | no assertion criteria provided | not provided | Converted during submission to Pathogenic. |