Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000085447 | SCV001215910 | pathogenic | not provided | 2023-10-15 | criteria provided, single submitter | clinical testing | This sequence change replaces aspartic acid, which is acidic and polar, with asparagine, which is neutral and polar, at codon 645 of the ABCA4 protein (p.Asp645Asn). This variant is present in population databases (rs61749418, gnomAD 0.004%). This missense change has been observed in individual(s) with Stargardt disease and retinitis pigmentosa (PMID: 9973280, 28559085, 29975949, 30029497, 31144483). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. ClinVar contains an entry for this variant (Variation ID: 99103). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt ABCA4 protein function. For these reasons, this variant has been classified as Pathogenic. |
Blueprint Genetics | RCV001074983 | SCV001240592 | pathogenic | Retinal dystrophy | 2017-11-12 | criteria provided, single submitter | clinical testing | |
Ce |
RCV000085447 | SCV001245786 | pathogenic | not provided | 2017-06-01 | criteria provided, single submitter | clinical testing | |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV004689454 | SCV005184466 | pathogenic | Retinitis pigmentosa | 2024-05-28 | criteria provided, single submitter | clinical testing | Variant summary: ABCA4 c.1933G>A (p.Asp645Asn) results in a conservative amino acid change located in the ABC-2 type transporter, transmembrane domain (IPR013525) of the encoded protein sequence. Four of five in-silico tools predict a damaging effect of the variant on protein function. The variant allele was found at a frequency of 2e-05 in 251094 control chromosomes. c.1933G>A has been reported in the literature in multiple compound heterozygous individuals affected with retinitis pigmentosa or Stargardt disease (e.g., Lewis_1999, Stone_2017, Wang_2018, Hu_2019). These data indicate that the variant is very likely to be associated with disease. The following publications have been ascertained in the context of this evaluation (PMID: 31543898, 9973280, 28559085, 30029497). ClinVar contains an entry for this variant (Variation ID: 99103). Based on the evidence outlined above, the variant was classified as pathogenic. |
Fulgent Genetics, |
RCV005025146 | SCV005661407 | pathogenic | Cone-rod dystrophy 3; Age related macular degeneration 2; Severe early-childhood-onset retinal dystrophy; Retinitis pigmentosa 19 | 2024-05-31 | criteria provided, single submitter | clinical testing | |
Retina International | RCV000085447 | SCV000117584 | not provided | not provided | no assertion provided | not provided |