Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Genetics and NGS Laboratory, |
RCV004699153 | SCV005201045 | likely pathogenic | Retinitis pigmentosa 19 | 2024-08-15 | criteria provided, single submitter | clinical testing | Hot-spot of length 17 amino-acids has 16 missense/in-frame variants (10 pathogenic variants, 6 uncertain variants and no benign), which qualifies as moderate pathogenic.UniProt protein ABCA4_HUMAN has 305 missense/in-frame variants (217 pathogenic variants, 88 uncertain variants and no benign), which qualifies as moderate pathogenic (PM1). GnomAD genomes homozygous allele count = 1. GnomAD exomes homozygous allele count = 1 (PM2).MetaRNN = 0.954 is greater than 0.939 ⇒ strong pathogenic (PP3).We identified this compound heterozygous variant in a 36-year-old woman diagnosed with retinitis pigmentosa. Her parents are not consanguineous. |