Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Institute of Human Genetics, |
RCV000408551 | SCV000281862 | likely pathogenic | Severe early-childhood-onset retinal dystrophy | 2016-01-01 | criteria provided, single submitter | clinical testing | |
Blueprint Genetics | RCV001075184 | SCV001240796 | pathogenic | Retinal dystrophy | 2018-11-05 | criteria provided, single submitter | clinical testing | |
Ce |
RCV000085563 | SCV001249467 | pathogenic | not provided | 2019-07-01 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000085563 | SCV001378534 | pathogenic | not provided | 2023-08-01 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This variant disrupts the p.Glu1087 amino acid residue in ABCA4. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 19265867, 22264887, 28559085, 30576320). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt ABCA4 protein function. ClinVar contains an entry for this variant (Variation ID: 99212). This missense change has been observed in individual(s) with Stargardt disease or cone-rod dystrophy (PMID: 19074458, 29555955). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. This variant is not present in population databases (gnomAD no frequency). This sequence change replaces glutamic acid, which is acidic and polar, with aspartic acid, which is acidic and polar, at codon 1087 of the ABCA4 protein (p.Glu1087Asp). |
MGZ Medical Genetics Center | RCV000408551 | SCV002579109 | likely pathogenic | Severe early-childhood-onset retinal dystrophy | 2022-04-01 | criteria provided, single submitter | clinical testing | |
Retina International | RCV000085563 | SCV000117700 | not provided | not provided | no assertion provided | not provided |