Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Blueprint Genetics | RCV001074273 | SCV001239846 | likely pathogenic | Retinal dystrophy | 2019-05-15 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000085817 | SCV003523290 | pathogenic | not provided | 2025-01-26 | criteria provided, single submitter | clinical testing | This sequence change replaces glutamic acid, which is acidic and polar, with lysine, which is basic and polar, at codon 2131 of the ABCA4 protein (p.Glu2131Lys). This variant is present in population databases (rs61750652, gnomAD 0.002%). This missense change has been observed in individual(s) with Stargardt disease (PMID: 9973280, 23143460, 30834176). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. ClinVar contains an entry for this variant (Variation ID: 99457). Invitae Evidence Modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) indicates that this missense variant is expected to disrupt ABCA4 protein function with a positive predictive value of 95%. For these reasons, this variant has been classified as Pathogenic. |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV004526616 | SCV005039830 | pathogenic | Stargardt disease | 2024-03-18 | criteria provided, single submitter | clinical testing | Variant summary: ABCA4 c.6391G>A (p.Glu2131Lys) results in a conservative amino acid change in the encoded protein sequence. Four of five in-silico tools predict a damaging effect of the variant on protein function. The variant allele was found at a frequency of 4e-06 in 251474 control chromosomes (gnomAD). c.6391G>A has been reported in the literature in multiple individuals affected with Stargardt Disease (e.g. Lewis_1999, Stone_2017). These data indicate that the variant is very likely to be associated with disease. The following publications have been ascertained in the context of this evaluation (PMID: 9973280, 28559085). ClinVar contains an entry for this variant (Variation ID: 99457). Based on the evidence outlined above, the variant was classified as pathogenic. |
Fulgent Genetics, |
RCV005031590 | SCV005656852 | pathogenic | Cone-rod dystrophy 3; Age related macular degeneration 2; Severe early-childhood-onset retinal dystrophy; Retinitis pigmentosa 19 | 2024-03-19 | criteria provided, single submitter | clinical testing | |
Retina International | RCV000085817 | SCV000117960 | not provided | not provided | no assertion provided | not provided |