Total submissions: 7
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000013301 | SCV000792874 | likely pathogenic | Autosomal recessive congenital ichthyosis 1 | 2017-07-19 | criteria provided, single submitter | clinical testing | |
Invitae | RCV000807794 | SCV000947868 | pathogenic | not provided | 2022-12-11 | criteria provided, single submitter | clinical testing | Experimental studies have shown that this missense change affects TGM1 function (PMID: 20663883, 22258055). For these reasons, this variant has been classified as Pathogenic. Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt TGM1 protein function. ClinVar contains an entry for this variant (Variation ID: 12483). This missense change has been observed in individuals with autosomal recessive congenital ichthyosis syndromes (PMID: 7824952, 9326318, 24314425, 26076875). This variant is not present in population databases (gnomAD no frequency). This sequence change replaces arginine, which is basic and polar, with cysteine, which is neutral and slightly polar, at codon 142 of the TGM1 protein (p.Arg142Cys). |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV001778651 | SCV002014973 | pathogenic | Lamellar ichthyosis | 2021-10-19 | criteria provided, single submitter | clinical testing | Variant summary: TGM1 c.424C>T (p.Arg142Cys) results in a non-conservative amino acid change located in the Transglutaminase, N-terminal domain (IPR001102) of the encoded protein sequence. Five of five in-silico tools predict a damaging effect of the variant on protein function. The variant was absent in 251442 control chromosomes. c.424C>T has been reported in the literature in multiple individuals affected with Lamellar Ichthyosis (example, Huber_1995, Laiho_1999, Mir-Bonafe_2015). These data indicate that the variant is very likely to be associated with disease. At least one publication reports experimental evidence evaluating an impact on protein function. The most pronounced variant effect results in <10% of normal Transglutaminase enzyme activity in vitro (example, Huber_1997). Two clinical diagnostic laboratories have submitted clinical-significance assessments for this variant to ClinVar after 2014 without evidence for independent evaluation. All laboratories classified the variant as pathogenic/likely pathogenic. Based on the evidence outlined above, the variant was classified as pathogenic. |
Genome- |
RCV000013301 | SCV002763995 | likely pathogenic | Autosomal recessive congenital ichthyosis 1 | criteria provided, single submitter | clinical testing | ||
Baylor Genetics | RCV000013301 | SCV004203812 | pathogenic | Autosomal recessive congenital ichthyosis 1 | 2024-01-01 | criteria provided, single submitter | clinical testing | |
OMIM | RCV000013301 | SCV000033548 | pathogenic | Autosomal recessive congenital ichthyosis 1 | 1997-09-01 | no assertion criteria provided | literature only | |
Natera, |
RCV000013301 | SCV002091236 | pathogenic | Autosomal recessive congenital ichthyosis 1 | 2020-08-13 | no assertion criteria provided | clinical testing |