Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000013121 | SCV000800575 | uncertain significance | Autosomal recessive DOPA responsive dystonia | 2017-08-11 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000013121 | SCV002238974 | pathogenic | Autosomal recessive DOPA responsive dystonia | 2023-10-17 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with histidine, which is basic and polar, at codon 337 of the TH protein (p.Arg337His). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individual(s) with infantile parkinsonism (PMID: 11246459). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. It has also been observed to segregate with disease in related individuals. This variant is also known as R306H. ClinVar contains an entry for this variant (Variation ID: 12328). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) has been performed at Invitae for this missense variant, however the output from this modeling did not meet the statistical confidence thresholds required to predict the impact of this variant on TH protein function. Experimental studies have shown that this missense change affects TH function (PMID: 15468323, 24753243). For these reasons, this variant has been classified as Pathogenic. |
Baylor Genetics | RCV000013121 | SCV004203870 | likely pathogenic | Autosomal recessive DOPA responsive dystonia | 2023-04-25 | criteria provided, single submitter | clinical testing | |
OMIM | RCV000013121 | SCV000033368 | pathogenic | Autosomal recessive DOPA responsive dystonia | 2000-01-01 | no assertion criteria provided | literature only |